Gene Therapy Approaches in Spinal Muscular Atrophy: Neurological Outcomes and Safety. Current Research in Neurology and Neurosurgery, [S. l.], v. 9, n. 1, p. 25–32, 2026. DOI: 10.5281/zenodo.22310567. Disponível em: https://somatopub.com/index.php/CRNN/article/view/424. Acesso em: 31 oct. 2026.